This story is part of a series on the current progression in Regenerative Medicine. This piece is part of a series dedicated to the eye and improvements in restoring vision. In 1999, I defined ...

Please provide your email address to receive an email when new articles are posted on . The loss of UBAP1L gene function appears to be associated with nonsyndromic retinal dystrophy, according to ...

LONDON and NEW YORK, Feb. 21, 2025 (GLOBE NEWSWIRE) -- MeiraGTx Holdings plc (Nasdaq: MGTX), a vertically integrated, clinical stage genetic medicines company, today announced the publication of ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy ...

Ophthalmic images from five of the patients in the study demonstrate significant variability in the forms of retinal dystrophy. Disclaimer: AAAS and EurekAlert! are not responsible for the accuracy of ...

Prime Medicine’s (PRME) treatment of retinal dystrophy due to USH2A gene mutations was granted FDA orphan designation, according to a post to the agency’s website. TipRanks is the most comprehensive ...

Scientists at the National Institutes of Health (NIH) and their colleagues have identified a gene responsible for some inherited retinal diseases (IRDs), which are a group of disorders that damage the ...

Collaborative effort will bring hope to BBS patients suffering from retinal degeneration through this investigational gene therapy. Bardet-Biedl Syndrome (BBS) is a genetic condition that causes multi ...

ATLANTA, May 5, 2025 /PRNewswire/ -- Odylia Therapeutics, a nonprofit (501(c)3) biotechnology company dedicated to advancing treatments for rare diseases, today announced its latest pipeline project: ...